Gene Therapy genes Genetic Disorders Skin-Cells-Turned-to-Heart-Cells Help Unravel Genetic Underpinnings of Cardiac Function By Staff Reports 2 months ago Genome-wide association studies have uncovered more than 500 genetic variants linked to heart function, everything
Biotechnology cancer Clinical Trials drug development Gene Therapy MicroRNA-based Therapy May be New Weapon to Combat Cancer By Staff Reports 3 months ago A technology that manipulates microRNAs (miRNAs) developed by Jingfang Ju, PhD, a biochemist and Professor
Biotechnology cancer Gene Therapy genes Genetic Disorders Genomes New research published in cancer discovery identifies new drug target for glioblastoma By Staff Reports 4 months ago A new international study co-led by Cleveland Clinic has identified a new drug target for
Biotechnology Gene Therapy genes rare diseases 3 Signs of Progress Against Sickle Cell Disease By Staff Reports 6 months ago A decade ago, the United Nations declared June 19 to be World Sickle Cell Awareness
Biotechnology Gene Therapy stem cells SIRT1 plays key role in chronic myeloid leukemia by aiding persistence of leukemic stem cells By Staff Reports 6 months ago Patients with chronic myeloid leukemia can be treated with tyrosine kinase inhibitors. While these effective
Gene Therapy Researchers Identify Causes and Mechanisms of Polycystic Ovary Syndrome Using Family-Based Genetic Analysis By Staff Reports 7 months ago A first-of-its-kind study using family-based genetic analysis has confirmed a gene involved in male hormone
cancer Cell Therapy Gene Therapy Genome-Wide Analysis Reveals New Strategies to Target Pancreatic Cancer By Staff Reports 8 months ago For some cancers, initial treatment with chemotherapy brings positive, but only temporary, results: tumors shrink,
Biotechnology Gene Therapy With gene therapy, University of Michigan Kellogg Eye Center targets rare form of childhood blindness. By Staff Reports 10 months ago Eye troubles detected at infancy began to take their toll when Emma Kate Roden started
Biotechnology Cell Therapy Gene Therapy genes Folliculin mutations disrupt embryo implantation By Staff Reports 10 months ago New information is unfolding on the genetic controls of an early turning point in pregnancy.
Gene Therapy Sangamo unveils interim gene therapy data: drug safe but not nearly enough to produce a meaningful clinical benefit By Staff Reports 10 months ago Sangamo Therapeutics, Inc. presented interim data from the Phase 1/2 EMPOWERS Study evaluating the SB-318
Biotechnology Clinical Trials Gene Therapy genes Proof of Concept Study Aims for Rapid Genotyping to Guide Epilepsy Treatment By Staff Reports 1 year ago An easy and inexpensive test for the HLA-B*15:02 allele could one day allow clinicians to
Gene Therapy Sarepta Therapeutics Presented Positive Preliminary Results from the First Three Children Dosed in the Phase 1/2a Gene Therapy Micro-dystrophin Trial to Treat Patients with Duchenne Muscular Dystrophy By Staff Reports 1 year ago Sarepta Therapeutics, Inc., a commercial-stage biopharmaceutical company focused on the discovery and development of precision
Biotechnology cancer Gene Therapy Immunotherapies CAR-T Immunotherapy Eliminates Metastatic Colorectal Cancer in Mice By Staff Reports 2 years ago Immunotherapy has given patients and oncologists new options, which for some patients, has meant cures
Biotechnology Gene Therapy Uncategorized Gene Therapy May Help Brain Heal From Stroke, Other Injuries By Staff Reports 2 years ago Scientists have found a genetic trigger that may improve the brain’s ability to heal from
Gene Therapy Mass. Eye and Ear Performs First FDA-Approved Gene Therapy Procedure for Inherited Disease By Staff Reports 2 years ago Massachusetts Eye and Ear made medical history this week by performing the first post-FDA approval
Gene Therapy New gene therapy corrects a form of inherited macular degeneration in canine model By Staff Reports 2 years ago Researchers from the University of Pennsylvania have developed a gene therapy that successfully treats a
Gene Therapy Gene Therapy Researchers Find a Viral Barcode to Cross the Blood-Brain Barrier By Staff Reports 2 years ago Gene therapies promise to revolutionize the treatment of many diseases, including neurological diseases such as
Biotechnology cancer Gene Therapy rare diseases IU Advances Fight Against Hepatitis B with ‘Virus-Cracking’ Molecules By Staff Reports 2 years ago Indiana University researchers have made an important step forward in the design of drugs that
Biotechnology Clinical Trials Gene Therapy Immunotherapies T Cell Therapy Shows Persistent Benefits in Young Leukemia Patients By Staff Reports 2 years ago CHOP Oncologists Update Analysis in Pivotal Global Trial of CAR T-Cell Treatment for Relapsed or
Gene Therapy Pharmaceutical Business News Abeona Receives FDA Regenerative Medicine Advanced Therapy Designation for Gene Therapy in Epidermolysis Bullosa By Staff Reports 2 years ago Gene therapy developer, Abeona Therapeutics, announced that the FDA has granted Regenerative Medicine Advanced Therapy