IntraBio Receives Niemann-Pick disease European Orphan Drug Designation for IB1000 Series
IntraBio Inc., a late-stage biopharmaceutical company developing novel therapies for rare "orphan" and common neurodegenerative diseases, announced that the European Commission has granted Orphan Medicinal Drug Designation for its lead compound series (IB1000s) for the treatment Niemann-Pick disease Type A, B and C. Niemann-Pick disease Type C (NPC) is a rare, devastating, neurovisceral autosomal-recessive inherited metabolic, lysosomal storage disorder (LSD) that predominately affects pediatric patients. Niemann-Pick disease Type C affects